Cell and gene therapy for blood disorders. Modeling of novel treatment strategies for Gaucher type 1 disease and Diamond-Blackfan anemia in mice.
Author
Summary, in English
In summary, this thesis focuses on translational and basic research evaluating novel cell and gene therapeutic strategies for GD type 1 and DBA.
Department/s
Publishing year
2015
Language
English
Publication/Series
Lund University Faculty of Medicine Doctoral Dissertation Series
Volume
2015:92
Document type
Dissertation
Publisher
Division of Molecular Medicine and Gene Therapy
Topic
- Cell and Molecular Biology
Keywords
- Gaucher disease
- lentiviral vectors
- gene therapy
- Diamond-Blackfan anemia
- hematopoietic stem cells
- bone marrow transplant
- Schlafen-2
Status
Published
Supervisor
- Stefan Karlsson
- Ulrika Blank Savukinas
- Göran Karlsson
ISBN/ISSN/Other
- ISSN: 1652-8220
- ISBN: 978-91-7619-171-2
Defence date
23 October 2015
Defence time
13:00
Defence place
Segerfalk lecture hall, BMC A10, Sölvegatan 17, Lund
Opponent
- Juan Bueren (Professor)